CRISPR genome editing clicks for amyloid cardiomyopathy. New @NEJM #AHA24 https://
nejm.org/doi/full/10.10
56/NEJMoa2412309
… A Phase 1 study with marked reduction of serum TTR @dr_m_fontana @ucl
CRISPR Genome Editing Shows Promise for Amyloid Cardiomyopathy
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